Medical Genetics Unit
Innovative Clinical Trials Clinic – Cona
In conjunction with the Paediatric Surgery Department, the Medical Genetics Unit is hosting innovative clinical trials of exon-skipping therapy for Duchenne muscular dystrophy. Currently two trials ongoing are under way: a phase I/IIa trial of exon 44 skipping, sponsored by the pharmaceutical company Prosensa Therapeutics BV, and a phase III trial of exon-51 skipping, sponsored by Glaxo Smith Kline.
(Cona - Amb. #12: Sector 3, Corps E, 1st floor – Tel: 239331- Fax: 239706).
(Cona Hospital, room 12, sector 3, building E, 1st floor, phone: 0039-0532-239705, fax: 0039-0532-239706).
For information e-mail: trialsgeneticamedica@unife.it
For more details please see this pdf presentation:



